Prescription drugs and vaccines revolutionized health care, dramatically decreasing death from disease and improving quality of life across the globe. But how do researchers, universities and ...

The Food and Drug Administration is proposing a system for approving customized drugs and medical treatments for patients with rare or hard-to-treat diseases.

The Food and Drug Administration may be one step closer to what could be the first approval of a drug that uses the groundbreaking gene-editing tool CRISPR. The drug, called exa-cel, treats sickle ...

A powerful new approach for the precise, flexible modification of a broad class of chemical compounds called bicyclic aza-arenes—which are commonly used to build drug molecules—has been developed. The ...

Combining precise genome engineering and protein activity profiling to methodically study thousands of cancer genes, scientists were able to pinpoint promising cancer drug targets. Searching for new ...

Researchers have successfully develop single-atom editing technology that maximizes drug efficacy. In pioneering drug development, the new technology that enables the easy and rapid editing of key ...

Some of the pioneering medical breakthroughs in recent history, including the first RSV vaccines and a first-of-its-kind gene therapy, have made it into the 2024 edition of the Drugs to Watch report ...

Instead of injecting weight-loss drugs every week, what if your body could make its own? In a study from the University of Osaka, researchers used genome editing to engineer mouse liver cells to ...

Scripps Research scientists combined two methods to study cysteine residues in proteins previously linked to cancer. Using chemical proteomics (top), they learned which cysteines were accessible to ...